alpha-Mannosidosis

alpha-Mannosidase Deficiency; Deficiencies, alpha-Mannosidase; Deficiency, alpha-Mannosidase; alpha Mannosidase Deficiency; alpha Mannosidosis; alpha-Mannosidase Deficiencies; alpha-Mannosidoses
An inborn error of metabolism marked by a defect in the lysosomal isoform of ALPHA-MANNOSIDASE activity that results in lysosomal accumulation of mannose-rich intermediate metabolites. Virtually all patients have psychomotor retardation, facial coarsening, and some degree of dysostosis multiplex. It is thought to be an autosomal recessive disorder.